About Us
We are an agile multi-stakeholder initiative aimed at supporting European Reference Networks (ERNs) to collaborate with stakeholders to pursue opportunities that will address unmet medical needs of people living with rare diseases.
Our Aim
Unlocking opportunities
Our aim is to unlock opportunities for partnerships, particularly with the pharmaceutical industry, in areas such as:
Basic to translational research
Clinical trials for rare & ultra-rare conditions
Testing and accelerating innovative approaches to diagnosis
Development and implementation of data/evidence generation initiatives