Our Work

Collaboration Case Studies

During the course of our work, stakeholders have shared with us examples of successful collaboration between clinical research networks and industry.

Together for Rare Diseases wants to use its platform to amplify these case studies, and promote the sharing of intelligence around how others have achieved success – for the benefit of the whole rare disease community.

Examples of clinical research and industry partnerships

TREAT-NMD

TREAT-NMD is a network for the neuromuscular field that provides an infrastructure to ensure that the most promising new therapies reach patients as quickly as possible. Since its launch in January 2007 the network’s focus has been on the development of tools that industry, clinicians and scientists need to bring novel therapeutic approaches through preclinical development and into the clinic, and on establishing best-practice care for neuromuscular patients worldwide.

Innovative Therapies for Children with Cancer in Europe (ITCC)

ITCC gathers 63 European Paediatric Oncology Departments with expertise in conducting early phase trials in children and adolescents, and 25 European research laboratories.

The aim of this organisation is to develop novel therapies for the treatment of paediatric and adolescent cancers in cooperation with regulatory bodies, pharmaceutical enterprises, parents and patients.

European Collaboration for Epilepsy Trials (ECET)

ECET is a non-for-profit organization registered in Ireland that brings together European professional and lay stakeholders associated with the International League Against Epilepsy (ILAE) and with the International Bureau for Epilepsy (IBE) to promote prevention, treatment and research of epilepsy.


Examples of registries that are involved in collaborations with industry

The European Society for Blood and Marrow Transplantation (EBMT) Registry

The EBMT Registry, established in 1974, is the backbone of the EBMT’s research and educational activities. As of 2021, the EBMT Registry has acquired data on over 700,000 patients that received a haematopoietic stem cell transplantation (HSCT) procedure procedure as well as data on over 3,000 patients that received CAR T-cell therapy.

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01 January at 12:00am